Explores the production of viral vectors for gene therapy applications, emphasizing AAV vectors and the process of large-scale production and purification.
Explores preclinical and clinical trials in SMA gene therapy, including efficiency in patients, trial results, adverse effects, cellular targeting, and future perspectives.
Explores pretraining sequence-to-sequence models with BART and T5, discussing transfer learning, fine-tuning, model architectures, tasks, performance comparison, summarization results, and references.