Concept

Gene gun

Related lectures (5)

Explores the production of viral vectors for gene therapy applications, emphasizing AAV vectors and the process of large-scale production and purification.

Obesity and Genetic Mutations: Impacts on Weight Regulation

Explores genetic mutations affecting weight regulation and gene expression in mice.

Choosing a Viral Vector and Delivery Method

Discusses viral vector selection for gene therapy, with a focus on AAV vectors for SMA1 therapy and CNS delivery.

Personalized Medicine: Gene Therapy and CRISPR

Explores personalized medicine, gene therapy, CRISPR technology, gene editing strategies, and ethical implications of synthetic genomics.

Gene Therapy: Neurological Diseases

Explores gene therapy for neurological diseases, including monogenic and multifactorial disorders, and the use of Cas9 and repair mechanisms.