Explores the historical aspects of drug development, regulatory agencies, and ethical principles in pharmacology, emphasizing the importance of informed consent and human subject protection.
Explores the challenges of inferring epidemiological parameters from clinical data, focusing on COVID-19 and the complexities of estimating infection fatality ratios.
Explores preclinical and clinical trials in SMA gene therapy, including efficiency in patients, trial results, adverse effects, cellular targeting, and future perspectives.